Tag Archives: Disease

PAH: An Under-Recognized Complication of Adult-Onset Still's Disease

January 11, 2019 This article originally appeared here. Share this content: PAH is an under-diagnosed complication of adult-onset Still disease. Pulmonary arterial hypertension (PAH) is a complication of adult-onset Still disease (AOSD) that in recent years has been recognized more frequently, indicating it is more common than originally documented, according to a retrospective study published… Read More »

With Gamifant launch rolling, Sobi unveils more data backing the rare disease med

SAN DIEGO—Armed with last month’s FDA approval, Sobi is rolling out its newly minted rare disease drug Gamifant with a small, targeted sales force, and Monday it unveiled more of the data that won the agency’s favor in the first place. In a phase 2/3 trial of Gamifant in primary haemophagocytic lymphohistiocytosis (HLH), 64.7% of… Read More »